NLRP3

NLR family pyrin domain-containing 3

Also known as: NLRP3, NALP3, cryopyrin, CIAS1

Biology & Mechanism

NLRP3 is an innate immune sensor that forms the NLRP3 inflammasome complex, leading to caspase-1 activation and processing of pro-IL-1β and pro-IL-18. In microglia, NLRP3 is activated by diverse damage signals including amyloid-beta fibrils, tau aggregates, and alpha-synuclein. NLRP3 inflammasome activation in microglia is implicated in neuroinflammation driving neurodegeneration. NLRP3 inhibitors are in clinical development for multiple inflammatory diseases.

Open Questions

  • Does NLRP3 activation in microglia represent a cause or consequence of neurodegeneration?
  • Can CNS-penetrant NLRP3 inhibitors provide therapeutic benefit in AD or PD patients?
  • Are there genetic variants in the NLRP3 pathway associated with neurodegeneration risk?

Sources

Evidence Status

human tissuesingle-cell RNA-seqanimal modelin vitro assayclinical program

Disease Links

  • Alzheimer's disease
  • Parkinson's disease
  • Amyotrophic lateral sclerosis
  • Multiple sclerosis
  • Traumatic brain injury

Related Targets

Last reviewed: June 1, 2026